Camp Open House

December 4th, 2014
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Our GHA open house is an open invitation to GHA members, and future campers interested in what we do at camp. The event is FREE and lunch is provided. Click here for more information.

Gene Therapy Study Still Succeeding 3 Years Later

December 4th, 2014
Posted in Uncategorized

It has now been three years since a group of patients with severe hemophilia B, or factor IX (FIX) deficiency, in London received a single dose of gene therapy as part of a new clinical trial. Early results of the trial were positive as these patients began to generate FIX levels ranging from 1%-6%. Prior to the study, they produced little to none of the crucial clotting factor protein. – Click here to read more.

Medical Advisory #417

December 4th, 2014
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Medical Advisory #417: Assessment of Possible Increased Risk of Inhibitors in Specific Recombinant FVIII Replacement Concentrates in Previously Untreated Patients (PUPS). Click here for more information.